Source Job

US

  • Support clinical trial recruitment and site outreach, coordinating feedback with clinical teams.
  • Establish scientific relationships with KOLs in the Duchenne community and refine KOL mapping.
  • Gather scientific insights and attend medical conferences as a Medical Affairs representative.

Medical Affairs Clinical Research Rare Disease Gene Therapy

18 jobs similar to Senior Medical Science Liaison - DMD/Neuromuscular (Southeast)

Jobs ranked by similarity.

US Unlimited PTO

  • Establish and maintain peer-to-peer relationships with regional and national KOLs in pediatric endocrinology and rare metabolic disorders.
  • Serve as a scientific expert, providing medical information and clinical support to advance launch readiness for multiple indication launches.
  • Collaborate with cross-functional teams to capture field insights, support medical congress activities, and ensure compliant scientific exchange.

Rezolute is a late-stage rare disease biopharmaceutical company developing transformative therapies for patients with severe metabolic and endocrine disorders. The company emphasizes scientific innovation, collaboration, and integrity as it prepares for multiple indication launches and builds its new Medical Affairs team.

US

  • Design and lead the U.S. field reimbursement team for the launch of deramiocel, a cell therapy for Duchenne muscular dystrophy.
  • Partner with payer strategy, hub vendor, and cross-functional teams to ensure compliant patient access and reimbursement.
  • Own field reimbursement SOPs, budget, and team performance while capturing insights to shape market access strategy.

Capricor Therapeutics is a biotechnology company advancing transformative cell and exosome-based therapies for rare diseases. It is a publicly traded, mission-driven organization with a collaborative culture focused on scientific rigor and execution.

$175,000–$220,000/yr
US

  • Serve as the primary point of contact for patients and caregivers, providing education on disease state, therapy options, and access pathways.
  • Coordinate access and reimbursement, including affordability enrollment, benefit verifications, prior authorization, and site-of-care logistics.
  • Collaborate with internal teams and external stakeholders to remove non-clinical barriers and enhance the patient experience.

Scholar Rock is a biopharmaceutical company developing muscle-targeted therapies for spinal muscular atrophy and other rare neuromuscular diseases. It leverages a proprietary platform to create novel monoclonal antibodies, with a strong commitment to innovation and patient support.

US

  • Establish and maintain peer relationships with key opinion leaders and act as the primary clinical/scientific resource to healthcare providers.
  • Support evidence generation initiatives, identify gaps in research, and report medical insights to inform strategy.
  • Attend medical conferences, respond to scientific requests, and ensure compliance with FDA regulations and company policies.

Regeneron is a leading biotechnology company that invents life-transforming medicines for people with serious diseases. Founded and led by physician-scientists for over 30 years, it has an award-winning culture and has produced multiple FDA-approved treatments.

$187,000–$265,000/yr

  • Develop and execute targeted engagement strategies for key accounts and treatment centers in the Central US region.
  • Lead regional business planning and collaborate with cross-functional teams to drive commercial launch readiness.
  • Serve as primary point of contact for stakeholders, ensuring alignment with corporate goals and market access strategies.

Since 2009, REGENXBIO has pioneered gene therapy, advancing a pipeline of treatments for rare and retinal diseases. Their growing, mission-driven team collaborates to develop transformative therapies for patients in need.

$245,000–$350,000/yr
US

  • Lead strategic engagement with payers, PBMs, and GPO accounts to secure patient access.
  • Develop market access strategies and negotiate contracts, including value-based models.
  • Build and oversee payer account teams while collaborating across functions.

REGENXBIO is a gene therapy company pioneering treatments for rare and retinal diseases. The company fosters a collaborative, patient-focused culture with a talented team working to make a meaningful difference for patients and their families.

$140,000–$160,000/yr
US

  • Create awareness about treatment options and support services through selling and promotional activities.
  • Engage healthcare providers via phone, email, video conferencing, and face-to-face.
  • Partner with patient support teams and collaborate with Marketing and Medical Affairs on education initiatives.

Cycle Pharmaceuticals is a pharmaceutical company focused on rare metabolic, immunological, and neurological genetic conditions, using cutting-edge drug delivery technologies. The company is headquartered in Cambridge, UK, with a significant US presence, and has been named one of the UK's fastest-growing private companies, fostering an entrepreneurial and patient-focused culture.

US Unlimited PTO

  • Develop and maintain senior payer relationships across a ten-state Northeast territory.
  • Lead account strategy for 16 accounts including Highmark, Independence, Point32Health, and UPMC.
  • Coordinate cross-functionally to resolve access barriers and support rare disease launches.

BridgeBio is a biopharmaceutical company using a 'moneyball for biotech' model to advance early-stage research and develop rare disease treatments. It values curiosity, experimentation, and boundary-pushing, fostering a collaborative culture with respected industry minds.

US Unlimited PTO

  • Serve as regional reimbursement expert, educating providers on access pathways and addressing barriers in commercial and government payer environments.
  • Coordinate family access and support, ensuring compliant education and seamless coordination among providers, pharmacies, and internal teams.
  • Act as a senior cross-functional partner, generating field insights and contributing to access strategy while mentoring colleagues.

BridgeBio pioneered a 'moneyball for biotech' approach, pooling early-stage research to reduce risk and unleash innovation for rare diseases. They value curiosity and experimentation, with a culture that defies convention and empowers problem-solvers.

$149,860–$181,595/yr
United States Unlimited PTO

  • Build scientific partnerships with thought leaders and HCPs to advance radiopharmaceutical therapies.
  • Lead high-impact scientific discussions and provide strategic input on clinical trials and evidence generation.
  • Synthesize real-world insights to inform clinical strategy and cross-functional teams.

RayzeBio, a Bristol Myers Squibb subsidiary, develops transformative radiopharmaceutical therapies for cancer. The company is led by an experienced entrepreneurial team and offers a collaborative culture where ideas are valued.

US

  • Provide field-based scientific expertise in GU Oncology, specifically non-muscle invasive bladder cancer.
  • Build and maintain scientific relationships with healthcare professionals and external experts.
  • Support Medical Affairs initiatives including advisory boards, congresses, and scientific exchange.

We are a global commercialization services company for the life sciences industry, helping bring innovative therapies to market. Our team of over 6,000 employees serves more than 650 clients, and we are proud to be a Great Place to Work.

$124,000–$155,000/yr
US 3w PTO

  • Provide expert field-based patient education and support throughout the treatment journey for the Rett community.
  • Serve as a dedicated point of contact for clinical education questions and resource needs for families and caregivers.
  • Collaborate with cross-functional partners to develop tools and enhance therapy management strategies.

Acadia is a pharmaceutical company dedicated to providing education and support to the Rett syndrome community through patient-centered programs. The company fosters a diverse and inclusive culture with competitive benefits and opportunities for growth.

US

  • Lead and develop a team of Medical Science Liaisons (MSLs) in a designated geographic region to achieve scientific and business objectives.
  • Coach and mentor MSLs to enhance their performance, scientific knowledge, and strategic impact.
  • Collaborate cross-functionally to align field activities with broader medical objectives and ensure compliance.

AbbVie is a global biopharmaceutical company dedicated to discovering and delivering innovative medicines for serious health issues in immunology, oncology, and neuroscience. They foster a collaborative and inclusive culture to drive scientific excellence.

$80,000–$90,000/yr
US

  • Build and maintain a network of specialist consultants and physicians to refer patients to clinical studies.
  • Identify opportunities to expand the local physician database and increase practices working with Care Access.
  • Maintain strong relationships with physicians and ensure high-quality customer service across the region.

Care Access brings clinical research and health services directly to communities through hundreds of locations and mobile clinics. They are dedicated to making the future of health better and more accessible for all.

$180,000–$230,000/yr
US

  • Serve as the primary field-based scientific expert engaging healthcare professionals to exchange clinical and research knowledge.
  • Build and maintain scientific relationships with HCPs, professional societies, and healthcare organizations in the Northern California territory.
  • Support clinical development, deliver training, and represent Sobi at medical conferences.

Sobi is a specialized biopharmaceutical company dedicated to developing and delivering innovative therapies for rare diseases. With over 1,900 employees in more than 30 countries, the company fosters a collaborative, inclusive culture focused on making a difference for patients.

$185,000–$230,000/yr
US Unlimited PTO

  • Serve as regional expert on reimbursement and access for BridgeBio therapies.
  • Educate providers on benefits investigation, prior authorization, and appeals.
  • Coordinate patient support across hubs, pharmacies, and internal teams.

BridgeBio is a biopharmaceutical company pioneering a 'moneyball for biotech' approach to pool early-stage research and develop life-changing medicines for rare diseases. It values curiosity and experimentation, with small expert teams empowered to solve problems.

US

  • Establish, grow, and lead the national field-based MSL team, defining operational frameworks and best practices.
  • Oversee field-based support of clinical trials and strategic engagement of key thought leaders.
  • Ensure high standards of scientific excellence and compliance with all applicable regulations.

Orca Bio is a commercial-stage biotechnology company redefining the transplant process by developing next-generation cell therapies for blood cancer patients. With a small, entrepreneurial team, they maintain a start-up culture of camaraderie and leadership by example.

Europe

  • Build and lead the DACH commercial field team, from pre-launch education to key account management.
  • Own launch plans for ADH1 and achondroplasia, including local marketing and forecasting.
  • Partner with Medical Affairs, Market Access, and Patient Advocacy for coordinated launch execution.

BridgeBio Pharma is a biotech that uses a 'moneyball' model to fund early-stage research and develop medicines for rare diseases and genetically driven cancers. It values curiosity, experimentation, and a hands-on culture, rewarding high performers.